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Adaptive and innovative study design in rare diseases

Arch Dis Child. 2024 Jun 5:archdischild-2024-327143. doi: 10.1136/archdischild-2024-327143. Online ahead of print.

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PMID:38839255 | DOI:10.1136/archdischild-2024-327143

By Nevin Manimala

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